This page uses Javascript. Your browser either doesn't support Javascript or you have it turned off. To see this page as it is meant to appear please use a Javascript enabled browser.
Print Document
Reports
Cover
Audit Information
Statements
Consolidated Balance Sheets
Consolidated Balance Sheets (Parenthetical)
Consolidated Statements of Operations and Comprehensive Loss
Consolidated Statements of Stockholders' Equity
Consolidated Statements of Stockholders' Equity (Parenthetical)
Consolidated Statements of Cash Flows
Reports
Nature of the Business and Basis of Presentation
Summary of Significant Accounting Policies
License, Collaboration, and Funding Agreements
Product Revenue, Net
Fair Value of Financial Assets and Liabilities
Inventory
Property and Equipment
Intangible Asset, Net
Accrued Expenses
Long-Term Debt
Leases
Commitment and Contingencies
Common Stock
Common Stock Warrants
Stock-Based Compensation
Income Taxes
Net Loss per Share
Gain on Sale of Nonfinancial Assets
Segment Information
Subsequent Events
Pay vs Performance Disclosure
Insider Trading Arrangements
Insider Trading Policies and Procedures
Accounting Policies
Summary of Significant Accounting Policies (Policies)
Tables
Summary of Significant Accounting Policies (Tables)
Product Revenue, Net (Tables)
Fair Value of Financial Assets and Liabilities (Tables)
Inventory (Tables)
Property and Equipment (Tables)
Intangible Asset, Net (Tables)
Accrued Expenses (Tables)
Long-Term Debt (Tables)
Leases (Tables)
Common Stock Warrants (Tables)
Stock-Based Compensation (Tables)
Income Taxes (Tables)
Net Loss per Share (Tables)
Segment Information (Tables)
Details
Nature of the Business and Basis of Presentation (Details)
Summary of Significant Accounting Policies - Schedule of Restricted Cash (Details)
Summary of Significant Accounting Policies - Schedule of Cash, Cash Equivalents and Restricted Cash (Details)
Summary of Significant Accounting Policies - Schedule of Property, Plant and Equipment (Details)
Summary of Significant Policies - Additional Information (Details)
License, Collaboration, and Funding Agreements - Genzyme Agreement (Details)
License, Collaboration, and Funding Agreements - Georgetown Agreement (Details)
License, Collaboration, and Funding Agreements - Beth Israel Deaconess Medical Center Agreements (Details)
License, Collaboration, and Funding Agreements - Research and Development Incentive Program (Details)
License, Collaboration, and Funding Agreements (Details)
Product Revenue, Net - Narrative (Details)
Product Revenue, Net - Product Reserve (Details)
Product Revenue, Net - Accounts Receivable Roll Forward (Details)
Fair Value of Financial Assets and Liabilities - Measured on a Recurring Basis (Details)
Fair Value of Financial Assets and Liabilities - Debt Securities Available-for-Sale (Details)
Fair Value of Financial Assets and Liabilities - Narrative (Details)
Fair Value of Financial Assets and Liabilities -Aggregate Fair Value of Warrant and Derivative Liabilities (Details)
Fair Value of Financial Assets and Liabilities - Assumptions (Details)
Fair Value of Financial Assets and Liabilities - Goodwill Rollforward (Details)
Inventory (Details)
Property and Equipment (Details)
Intangible Asset, Net - Narrative (Details)
Intangible Asset, Net - Future Amortization (Details)
Accrued Expenses (Details)
Long-Term Debt - Schedule of Long-Term Debt (Details)
Long-Term Debt - Narrative (Details)
Long-Term Debt - Hercules Loan Agreements (Details)
Long-Term Debt - Future Principal Payments (Details)
Leases (Details)
Leases - Schedule of Components of Lease Expense (Details)
Leases - Schedule of Maturities of Lease Liabilities (Detail)
Commitment and Contingencies (Details)
Common Stock (Details)
Common Stock Warrants - Additional Information (Details)
Common Stock Warrants - Schedule of Outstanding Warrants (Detail)
Common Stock Warrants - Summary of Outstanding Warrants to Purchase Shares of Common Stock (Details)
Stock-Based Compensation - Additional Information (Details)
Stock-Based Compensation - Summary of Stock Option Activity (Detail)
Stock-Based Compensation - Restricted Stock Units (Details)
Stock-Based Compensation - Summary of Stock-Based Compensation Expense Classification (Details)
Stock-Based Compensation - Stock Option Valuation (Details)
Stock-Based Compensation - Stock Appreciation Rights (Details)
Income Taxes - Narrative (Details)
Income Taxes - Schedule of Income Loss Before Income Taxes (Details)
Income Taxes - Reconciliation of Effective Income Tax Rate (Details)
Income Taxes - Deferred Income Tax Asset (Details)
Income Taxes - Deferred Tax Valuation Allowance (Details)
Income Taxes (Details)
Net Loss per Share - Summary of Basic and Diluted Net loss per Share Attributable to Common Stockholders (Details)
Net Loss per Share - Additional Information (Details)
Net Loss per Share - Schedule of Anti-dilutive Securities Excluded from Computation of Diluted Net Loss per Share Attributable to Common Stockholders (Details)
Loss on Transfer of Nonfinancial Assets - Additional Information (Details)
Segment Reporting (Details)
Segment Reporting - Other Segment Disclosures (Details)
Subsequent Events (Details)
All Reports